The safety and effectiveness of genetically corrected iPSCs derived from β-thalassaemia patients in nonmyeloablative β-thalassaemic mice
Our study provides evidence that the transplantation of genetically corrected, patient-specific iPSCs could be used to cure genetic diseases, such as β-thalassaemia major.
|Authors||Xian Y, Xie Y, Song B, Ou Z, Ouyang S, Xie Y, Yang Y, Xiong Z, Li H, Sun X|
|Journal||Stem cell research & therapy|
|Publication Date||2020 Jul 16;11(1):288|