Potential Binding Sites of Pharmacological Chaperone NCGC00241607 on Mutant β-Glucocerebrosidase and Its Efficacy on Patient-Derived Cell Cultures in Gaucher and Parkinson’s Disease

Authors Kopytova A, Rychkov G, Cheblokov A, Grigor’eva E, Nikolaev M, Yarkova E, Sorogina D, Ibatullin F, Baydakova G, Izyumchenko A, Bogdanova D, Boitsov V, Rybakov A, Miliukhina I, Bezrukikh V, Salogub G, Zakharova E, Pchelina S, Emelyanov A.
Journal Int J Mol Sci
Publication Date 2023-05-01

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