Understanding and Rescuing the Splicing Defect Caused by the Frequent ABCA4 Variant c.4253+43G>A Underlying Stargardt Disease

Authors	Suárez-Herrera Nuria, Garanto Alejandro, Collin Rob W.J.
Journal	Nucleic Acid Therapeutics
Publication Date	2024-04-01
DOI	10.1089/nat.2023.0076