Identification of AAV serotypes for gene therapy in Krabbe iPSCs-derived brain organoids
| Authors | Lv Y, Cui Z, Li H, Wang J, Wei M, Hu Y, Li X, Cao C, Zhang Y, Wang W |
|---|---|
| Journal | Genes & diseases |
| Publication Date | 2025 Jan;12(1):101269 |
| PubMed | 39534572 |
| PubMed Central | PMC11555342 |
| DOI | 10.1016/j.gendis.2024.101269 |