Identification of AAV serotypes for gene therapy in Krabbe iPSCs-derived brain organoids
Authors | Lv Y, Cui Z, Li H, Wang J, Wei M, Hu Y, Li X, Cao C, Zhang Y, Wang W |
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Journal | Genes & diseases |
Publication Date | 2025 Jan;12(1):101269 |
PubMed | 39534572 |
PubMed Central | PMC11555342 |
DOI | 10.1016/j.gendis.2024.101269 |