Identification of a histone deacetylase inhibitor as a therapeutic candidate for congenital central hypoventilation syndrome
| Authors | Africano Chiara, Bachetti Tiziana, Uva Paolo, Pitollat Gabriel, Del Zotto Genny, Giacopelli Francesca, Recchi Giada, Lenfant Nicolas, Madani Amélia, Beckouche Nathan, Thoby-Brisson Muriel, Ceccherini Isabella |
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| Journal | Molecular Therapy - Nucleic Acids |
| Publication Date | 2024-12-00 |
| DOI | 10.1016/j.omtn.2024.102319 |