CRISPR/Cas-Based Ex Vivo Gene Therapy and Lysosomal Storage Disorders: A Perspective Beyond Cas9
| Authors | Leal Andrés Felipe, Prieto Luis Eduardo, Pachajoa Harry |
|---|---|
| Journal | Cells |
| Publication Date | 2025-07-25 |
| DOI | 10.3390/cells14151147 |
| Authors | Leal Andrés Felipe, Prieto Luis Eduardo, Pachajoa Harry |
|---|---|
| Journal | Cells |
| Publication Date | 2025-07-25 |
| DOI | 10.3390/cells14151147 |