Gene augmentation therapy restores vision and preserves photoreceptors in a mouse model of CNGA1-retinitis pigmentosa

Authors Wu Yidong, Zhao Tianyuan, Wang Yazhi, Zhang Ting, Hang Chenyue, Wang Yafang, Liu Yang, Chen Zhixuan, Chen Jieqiong, Li Tong, Sun Junran, Jia Huixun, Zhang Lei, Wang Fenghua, Wan Xiaoling, Sun Xiaodong
Journal Communications Medicine
Publication Date 2025-09-02
DOI 10.1038/s43856-025-01108-x

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