Modeling Mowat-Wilson syndrome with patient iPSCs reveals transcriptional and phenotypic defects in neural progenitors

Authors Musante Ilaria, Gorrieri Giulia, Tamburro Serena, Ferrera Giulia, Baldassari Simona, Fetta Anna, Caraffi Stefano Giuseppe, Vignoli Aglaia, Fiorito Giovanni, Garavelli Livia, Canevini Maria Paola, Cordelli Duccio Maria, Zara Federico, Ricci Emilia, Scudieri Paolo
Journal Neurobiology of Disease
Publication Date 2026-01-00
DOI 10.1016/j.nbd.2025.107205

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