RNA
‐Based Therapies for Inherited Metabolic Disorders
| Authors | Vootukuri Reddy Sreekanth, Gurung Sonam, Ghosh Roopkatha, Mills Philippa B., Baruteau Julien, Zhou Haiyan |
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| Journal | Journal of Inherited Metabolic Disease |
| Publication Date | 2026-03-00 |
| DOI | 10.1002/jimd.70150 |