Generation of isogenic gene-corrected cell lines from a USH2A-RP patient-derived iPS cell line

Authors Del Buey Furió Verónica, García-Bohórquez Belén, García-García Gema, Gallardo M. Esther, Gamundi María José, Ellederova Zdenka, Ayuso Carmen, Millán José M., Erceg Slaven, Lukovic Dunja
Journal Stem Cell Research
Publication Date 2026-10-00
DOI 10.1016/j.scr.2026.104094

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