Generation of isogenic gene-corrected cell lines from a USH2A-RP patient-derived iPS cell line
| Authors | Del Buey Furió Verónica, García-Bohórquez Belén, García-García Gema, Gallardo M. Esther, Gamundi María José, Ellederova Zdenka, Ayuso Carmen, Millán José M., Erceg Slaven, Lukovic Dunja |
|---|---|
| Journal | Stem Cell Research |
| Publication Date | 2026-10-00 |
| DOI | 10.1016/j.scr.2026.104094 |