Generation of two NAGLU-mutated homozygous cell lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo B syndrome

Authors Benetó N, Cozar M, Gort L, Pacheco L, Vilageliu L, Grinberg D, Canals I
Journal Stem cell research
Publication Date 2019 Nov 29;42:101668
PubMed 31825816
DOI 10.1016/j.scr.2019.101668

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