Generation of two NAGLU-mutated homozygous cell lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo B syndrome
| Authors | Benetó N, Cozar M, Gort L, Pacheco L, Vilageliu L, Grinberg D, Canals I |
|---|---|
| Journal | Stem cell research |
| Publication Date | 2020 Jan;42:101668 |
| PubMed | 31825816 |
| DOI | 10.1016/j.scr.2019.101668 |