CRISPR-mediated correction of skeletal muscle Ca2+handling in a novel DMD patient-derived pluripotent stem cell model
| Authors | Morera Cristina, Kim Jihee, Paredes-Redondo Amaia, Nobles Muriel, Rybin Denis, Moccia Robert, Kowala Anna, Meng Jinhong, Garren Seth, Liu Pentao, Morgan Jennifer E, Muntoni Francesco, Christoforou Nicolas, Owens Jane, Tinker Andrew, Lin Yung-Yao |
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| Publication Date | 2022-02-18 |
| DOI | 10.1101/2022.02.17.480850 |