Correction of a CADASIL point mutation using adenine base editors in hiPSCs and blood vessel organoids
| Authors | Wang Jingwen, Zhang Lei, Wu Guanglan, Wu Jinni, Zhou Xinyao, Chen Xiaolin, Niu Yongxia, Jiao Yiren, Liu Qianyi, Liang Puping, Shi Guang, Wu Xueqing, Huang Junjiu |
|---|---|
| Journal | Journal of Genetics and Genomics |
| Publication Date | 2024-02-00 |
| DOI | 10.1016/j.jgg.2023.04.013 |