A novel iPSC model reveals selective vulnerability of neurons in multiple sulfatase deficiency

Authors Pham Vi, Sertori Finoti Livia, Cassidy Margaret M., Maguire Jean Ann, Gagne Alyssa L., Waxman Elisa A., French Deborah L., King Kaitlyn, Zhou Zitao, Gelb Michael H., Wongkittichote Parith, Hong Xinying, Schlotawa Lars, Davidson Beverly L., Ahrens-Nicklas Rebecca C.
Journal Molecular Genetics and Metabolism
Publication Date 2024-02-00
DOI 10.1016/j.ymgme.2023.108116

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