AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype

Authors	Boon N, Lu X, Andriessen CA, Moustakas I, Buck TM, Freund C, Arendzen CH, Böhringer S, Boon CJF, Mei H, Wijnholds J
Journal	Stem cell reports
Publication Date	2023 Jun 13;18(6):1388
PubMed	37315526
PubMed Central	PMC10277829
DOI	10.1016/j.stemcr.2023.05.008