A Novel AAV Capsid-Mediated RS1 Gene Therapy Restored Retinal Function to Wild-Type Levels in Rs1R213W Mouse Model

Authors Wei Xing, Ma Sisi, Zhou Yunyu, Cui Haoliang, Zhang Shan, Wang Duanyang, Fu Yingying, Li Wei, Han Huihui, Li Yamei, Li Wuyi, Liu Huixin, Sun Zixi, Han Xiaoxu, Zou Xuan, Li Hui, Wang Cheng, Sui Ruifang
Journal Investigative Ophthalmology & Visual Science
Publication Date 2025-04-15
DOI 10.1167/iovs.66.4.37

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