PRPF8 Mutation-Induced Defects in Human iPSC-Derived RPE Are Rescued by Adenine Base Editing

Authors Sun Xihao, Liang Yuan, Liang Yuqin, Li Wenwei, Chen Hang, Ding Chengcheng, Duan Chunwen, Zhou Yalan, Zhang Ruting, Xu Huizhuo, Chen Jiansu
Journal Investigative Ophthalmology & Visual Science
Publication Date 2026-01-09
DOI 10.1167/iovs.67.1.21

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