PRPF8 Mutation-Induced Defects in Human iPSC-Derived RPE Are Rescued by Adenine Base Editing
| Authors | Sun Xihao, Liang Yuan, Liang Yuqin, Li Wenwei, Chen Hang, Ding Chengcheng, Duan Chunwen, Zhou Yalan, Zhang Ruting, Xu Huizhuo, Chen Jiansu |
|---|---|
| Journal | Investigative Ophthalmology & Visual Science |
| Publication Date | 2026-01-09 |
| DOI | 10.1167/iovs.67.1.21 |