Astrocytes differentiated from patient iPSCs model the rare leukodystrophy MLC and uncover disease-linked maturation defects and Kir4.1 channel dysfunction
| Authors | Lanciotti Angela, Brignone Maria Stefania, De Nuccio Chiara, Sposito Sara, Caprini Elena Sofia, Belfiore Marcello, Nicita Francesco, Veroni Caterina, Meloni Chiara, Carrozzo Rosalba, Rizza Teresa, Aiello Chiara, Sartorelli Jacopo, Bertini Enrico, Visentin Sergio, Ambrosini Elena |
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| Journal | Neurobiology of Disease |
| Publication Date | 2026-01-00 |
| DOI | 10.1016/j.nbd.2025.107218 |