Generation and characterization of a novel Gaa compound heterozygous mouse model recapitulating human Pompe disease
| Authors | Huang Wenjun, Wang Jie, Zhou Yafei, Xiao Hongyu, Jiang Kaichong, Cui Jiale, Zhang Yanmin, Zhou Rui |
|---|---|
| Journal | Orphanet Journal of Rare Diseases |
| Publication Date | 2026-02-25 |
| DOI | 10.1186/s13023-026-04273-x |