Nucleoside‐Modified mRNA Encoding Alpha‐Galactosidase A Ameliorates Fabry Disease Phenotypes in Human IPSC‐Derived Cardiomyocytes

Authors	Juchem Malte, Oehlsen Lea, Ersoy Sedef, Ye Jia Li, Weber Natalie, Mohr Elisa, Agyapong Wilson, Liu Junqing, Fuchs Maximilian, Xiao Ke, Jahn Christopher, Eggenschwiler Reto, Cantz Tobias, Beimdiek Julia, Buettner Falk F. R., Kraft Theresia, Hegermann Jan, Knorr Ivonne J., Ernst Lisa, Feldbrügge Linda, Puffert Resa, Schmidt Kevin, Bär Christian, Hoepfner Jeannine, Thum Thomas
Journal	Advanced Science
Publication Date	2026-08-13
PubMed	42591063
PubMed Central	PMC13470294
DOI	10.1002/advs.77151