Generation of two compound heterozygous HGSNAT-mutated lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo C syndrome

Authors Benetó N, Cozar M, García-Morant M, Creus-Bachiller E, Vilageliu L, Grinberg D, Canals I
Journal Stem cell research
Publication Date 2019 Dec;41:101616
PubMed 31731183
DOI 10.1016/j.scr.2019.101616

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