Generation of two compound heterozygous HGSNAT-mutated lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo C syndrome

Authors	Benetó N, Cozar M, García-Morant M, Creus-Bachiller E, Vilageliu L, Grinberg D, Canals I
Journal	Stem cell research
Publication Date	2019 Dec;41:101616
PubMed	31731183
DOI	10.1016/j.scr.2019.101616