Altered lysosomal biology impairs motor neuron survival via TFEB dysregulation in spinal muscular atrophy

Authors Rosignol Ines, Dokuzluoglu Zeynep, Caldarelli Antonio, Oprişoreanu Ana-Maria, Ushakova Sofiia, Siddiqui Tohid, Grover Rahul, Guerlich Hannes, Falkenburger Björn, Diez Stefan, Grass Tobias, Becker Catherina G., Rodriguez-Muela Natalia
Publication Date 2025-07-10
DOI 10.1101/2025.07.07.663525

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